Muscles make up nearly 40% of the human body and power every move we make, from a child's first steps to recovery after ...
Dr. Rebecca Ahrens-Nicklas and Dr. Kiran Musunru crafted a bespoke treatment that has successfully corrected the genetic ...
The recent clinical success of treating “Baby KJ” Muldoon—an infant born with a rare metabolic disease—with the first-ever personalized gene-editing therapy brought much-needed enthusiasm to the ...
Vertex executives warned that Casgevy, its curative treatment for sickle cell disease, would be slow to reach patients. But ...
Torie Bosch is the First Opinion editor at STAT. Celena Lozano’s son Benny, who turned 5 in November, loves trains, trucks — anything that goes. He also has a rare disease, PURA syndrome. Earlier this ...
Vertex Pharmaceuticals and Orum Therapeutics are striking a deal to make new conditioning drugs for patients going on the Boston biotech's gene editing treatment, Casgevy. This story was originally ...
Using CRISPR, Hebrew University of Jerusalem team finds PEDS1 enzyme linked to reduced brain size; study maps 331 genes ...
Philadelphia and New Orleans, May 15, 2025 – In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing ...
Berkeley—Nobel Laureate Jennifer Doudna, PhD, professor of biochemistry, biophysics, and structural biology at UC Berkeley, aspires for “CRISPR to become the standard of medical care for certain ...
PHILADELPHIA and NEW ORLEANS, May 15, 2025 /PRNewswire/ -- In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results